Gene Therapy Multi-Dose Clinical Trial.

I am delighted to say that the Wave 1 trial is proceeding well.

We now have approximately 70 CF subjects who have received at least one dose of gene therapy, whilst some are up to the tenth of their allocated twelve monthly doses. The trial has been, as planned, reviewed twice so far by the Safety Committee who had no concerns about progress.

We still have room for anyone wishing to participate; please contact either Clare Saunders in London or Maria Dewar in Edinburgh for details. Much as we would like to know about how people are doing on the trial, no analysis of the data is allowed until we reach the end of the study. At present the last patient's data should become available to us around June next year.

Professor Eric Alton, March 2013

There is still an opportunity to be involved in the study as we will continue to recruit CF patients until the middle of June this year.

Places are available if:-

You live in the UK and are 12 years or older
You can make monthly visits to Edinburgh or London for approximately 13 months
You meet other inclusion criteria
For more information and conditions read this.

Patient Identification Centres.

To aid the enrollment process we are creating Patient Identification Centres at CF Clinics throughout the UK. More will be added over the next few weeks but if you are a patient at one of these clinics then they have already been briefed on the clinical trial inclusion criteria and the next steps in your enrollment process.

Clinical Trial Frequently Asked Questions.

If you have any general queries regarding the Clinical Trial then hopefully we can answer them here.

Or you can submit a question to our clinical teams here.