• GL67A/pGM169 - the clinical trial product
• The Clinical Teams
• The Tracking Study
• The Run-in Study
• Single Dose Clinical Trial (2009-2011)
• Multi Dose Clinical Trial (2012)

Multi-dose Clinical Trial

Our ultimate aim is to conduct a clinical trial over a long enough time period that we could look for and hope to see clinical benefit. The exact design of this study is not certain yet, and will be influenced by the findings in our single dose pilot study.

However, we are planning to include over 100 patients from the Run-in study, who will be asked to proceed based on the results of their measurements. Unlike the pilot study, this will be a blinded, placebo-controlled study, meaning that each participant will have a 50:50 chance of receiving gene therapy or 'dummy' treatment, with neither patients nor investigators knowing which.

As the timing of this trial depends critically on the results of the pilot safety study, this webpage will be updated once we have further information.

More information on the Run-in study patient groups we hope will go forward to the multi-dose trial can be found on the patient info page of this website.