Gene therapy is a largely experimental approach to treat diseases that have an underlying genetic cause.
Many diseases such as cystic fibrosis, muscular dystrophy, haemophilia and cancer are caused by faulty genes.
Gene therapy involves the addition of a healthy, working copy of the gene into appropriate cells in the body to replace or override the faulty copy present in the genome.
Unlike most conventional medicines, instead of treating the symptoms of a disease, gene therapy has the potential to correct the underlying cause.
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