A Phase IIb double-blind, placebo-controlled trial of non-viral mediated gene therapy for cystic fibrosis.

Secreted Gaussia Luciferase Is a More Sensitive Reporter Than Firefly Luciferase for Non- Viral Gene Transfer to Airway Epithelium Ex Vivo and In Vivo.
Griesenbach U et al.
The American Society of Gene Therapy Annual Conference (2009)

A clinical study to evaluate the safety and efficacy of pGM169/GL67A administered to the nose and lungs of individuals with cystic fibrosis.
Hyde SC et al.
The American Society of Gene and Cell Therapy Annual Conference (2010)

Assessment of F/HN-Pseudotyped Lentivirus in a Clinically Relevant Vector for Lung Gene Therapy
Griesenbach U et al.
The North American Cystic Fibrosis Conference (2012)

Self-Reactive T Cells to CFTR in Cystic Fibrosis (CF) and Non-CF Humans: Implications for Gene Therapy.
Limberis MP et al.
The American Society of Gene and Cell Therapy Annual Conference (2011)

The nuclear pore dilating Agent TCHD increases gene transfer into differentiated airway epithelium ex vivo, but has no efect in vivo.
Griesenbach U et al.
The American Society of Gene and Cell Therapy Annual Conference (2011)

Immune Responses to Single and Repeated Administration of pGM169/GL67A, The UK CF Gene Therapy Consortium Clinical Trials.
Griesenbach U et al.
British Thoracic Society Winter Meeting (2014)