Gene Therapy Clinical Trial Results to be Announced on 30th May

Wednesday, May 13th 2015

Print this page

Consortium_logo_small.jpgWe wanted to update you on the Multidose Gene Therapy Trial.

This was a complex trial requiring extensive data analysis, but we now have the results, which have been submitted for peer review. We wanted to share our findings with the CF community as soon as possible, so in collaboration with the CF Trust, we will be holding an open meeting to present the data and address questions.

This will be held in London on Saturday May 30th, and will be live-streamed for those unable to attend; we are also looking into the possibility of a simultaneous conference link to Edinburgh.

Unfortunately, for cross-infection reasons, we request that CF patients do not attend the venues.

To allow us to book the appropriately sized venues, it would be very helpful if those wishing to attend in person could indicate a preference for London or Edinburgh by following the link to the CF Trust website and filling in your details.

Further details of the venue and exact timing and information regarding the live streaming will be posted shortly.


Update, Thursday 14 May.

Shortly after the meeting, we will let all trial participants know whether they received the active gene therapy or the placebo and to provide contact details for any questions arising.

Many thanks once again to all of you for your invaluable help!


A CFTR Western blot, to confirm protein production in cell culture.


Proposed 3D model of the CFTR protein.