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The UK Cystic Fibrosis Gene Therapy Consortium
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GL67A pGM169 - Our first clinical trial product
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Papers 2
Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis
Alton EW et al., Thorax. 2017 Feb;72(2):137-147. doi: 10.1136/thoraxjnl-2016-208406.
A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis.
Alton EW et al., Efficacy and Mechanism Evaluation (2016) Volume: 3 Issue: 5
Abstracts 1
Moving lentiviral-based gene therapy into a first-in-man CF trial.
Griesenbach U et al.,The North American Cystic Fibrosis Conference (2015)
Bacterial Lysate (2009): Neutralisation of a bacterial lysate.
More...
DNA fragments being cut from an agarose gel exposed to UV.